There is no cure for NP-C and until recently, management strategies for the disease were based on non-specific, symptomatic treatments. These therapies may be at least partially successful in treating some symptoms of NP-C, but have no impact on disease progression or long-term outcomes. Symptoms that can be treated with general therapies include, but are not limited to:

  • Gelastic cataplexy - can be treated by using tricyclic antidepressants or CNS stimulants
  • Dystonia - can be treated by using anti-cholinergic drugs
  • Movement restrictions - can be treated by using physical therapy
  • Seizures - can be controlled by using anti-epileptic drugs
  • Feeding problems resulting from difficulty in swallowing - can be managed with a feeding tube

Zavesca is indicated for the treatment of progressive neurological manifestations in adult patients and pediatric patients with Niemann-Pick type C disease.

 

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Please note that the information contained in this section of the website is not intended for US residents. Please visit our US webpage.

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